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Article Dans Une Revue Human Gene Therapy Année : 2023

Limitations of Dual-Single Guide RNA CRISPR Strategies for the Treatment of Central Nervous System Genetic Disorders

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Neurobiologie

Dates et versions

hal-04453910 , version 1 (12-02-2024)

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Fábio Duarte, Gabriel Vachey, Nicholas Caron, Melanie Sipion, Maria Rey, et al.. Limitations of Dual-Single Guide RNA CRISPR Strategies for the Treatment of Central Nervous System Genetic Disorders. Human Gene Therapy, 2023, 34 (17-18), pp.958-974. ⟨10.1089/hum.2023.109⟩. ⟨hal-04453910⟩
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