Assessment of adeno-associated virus gene therapies efficacy on acid alpha-glucosidase restoration and glycogenstorage correction in cardiac muscle of Pompe disease mice using synchrotron infrared and ultravioletmicrospectroscopies
Résumé
Assessment of adeno-associated virus gene therapies efficacy on acid alpha-glucosidase restoration and glycogenstorage correction in cardiac muscle of Pompe disease mice using synchrotron infrared and ultravioletmicrospectroscopies