Assessment of adeno-associated virus gene therapies efficacy on acid alpha-glucosidase restoration and glycogen storage correction in cardiac muscle of Pompe disease mice using synchrotron infrared and ultraviolet microspectroscopies
Résumé
Assessment of adeno-associated virus gene therapies efficacy on acid alpha-glucosidase restoration and glycogen
storage correction in cardiac muscle of Pompe disease mice using synchrotron infrared and ultraviolet
microspectroscopies